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Table 1 Example of GAS goal topics and scores in (fictitious) patients with mitochondrial disease

From: Goal attainment scaling as an outcome measure in rare disease trials: a conceptual proposal for validation

Goals-2 score0 score (expected outcome level)+ 2 score
Being able to cook for me and my partnerThe patient cooks once a week or lessThe patient cooks three times a weekThe patient cooks five times a week or more
Being able to watch a film at night without falling asleepThe patient can watch a series episode of 25 min without falling asleepThe patient can watch a series episode of 50 min without falling asleepThe patient can watch a film of 2 h without falling asleep
Being able to dress myself independentlyThe patient needs help with putting on a shirt and pantsPatient can put on a shirt, but needs help with pantsThe patient can dress him/herself without any help